脊髓性肌萎缩-话题@MedSci

#脊髓性肌萎缩#

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脊髓性肌萎缩

2020-05-29

梅斯管理员 (审核中...)

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#儿童# #基因治疗# #营养支持# #脊髓性肌萎缩# #神经肌肉疾病# #运动功能# #呼吸支持# #真实世界研究#

JAMA子刊：SMA1患儿基因治疗2年营养支持率远低于Nusinersen，运动功能改善相当

2025-10-20发表于上海

梅斯管理员 (审核中...)

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#脊髓性肌萎缩# #康复管理#

脊髓性肌萎缩患者的康复管理

2025-07-18发表于上海

soongzhihua (审核中...)

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#脊髓性肌萎缩#

锦篮基因GC101治疗1型脊髓性肌萎缩症显示巨大潜力！

2023-01-22

soongzhihua (审核中...)

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#脊髓性肌萎缩#

中国脊髓性肌萎缩症呼吸管理专家研讨会成功落幕

2022-04-11

soongzhihua (审核中...)

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#脊髓性肌萎缩#

英国NICE 推荐 risdiplam 治疗脊髓性肌萎缩症

2021-12-14

soongzhihua (审核中...)

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#脊髓性肌萎缩#

“脊髓性肌萎缩症康复管理”专家第二次研讨会于线上顺利举办

2022-09-05

soongzhihua (审核中...)

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#脊髓性肌萎缩#

大咖云集，深度聚焦 | 中国脊髓性肌萎缩症康复管理专家研讨会在武汉成功召开

2022-01-23

soongzhihua (审核中...)

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#脊髓性肌萎缩#

1348万Zolgensma，一针治愈遗传病脊髓性肌萎缩症（SMA）

2022-12-02

soongzhihua (审核中...)

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#脊髓性肌萎缩#

JNNP：采用疾病改良疗法筛查新生儿脊髓性肌萎缩症的成本效果分析

2021-11-05

soongzhihua (审核中...)

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#脊髓性肌萎缩#

NEJM：基因疗法Evrysdi（risdiplam）治疗1型脊髓性肌萎缩婴儿，取得阳性数据

2021-03-15

soongzhihua (审核中...)

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#脊髓性肌萎缩#

Lancet Neurology：onasmonogene abeparvovec治疗有症状的婴儿型脊髓性肌萎缩症患者的3期临床试验

2021-08-13

soongzhihua (审核中...)

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#脊髓性肌萎缩#

Lancet Neurol：基因替代疗法治疗婴儿症状性脊髓性肌萎缩症1型的有效性与安全性？

2022-08-27

soongzhihua (审核中...)

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#脊髓性肌萎缩#

群英荟萃，深度聚焦：中国脊髓性肌萎缩症呼吸管理专家研讨会成功召开

2022-09-01

soongzhihua (审核中...)

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#脊髓性肌萎缩#

JNNP：诺西那生钠治疗新生儿至青年1型脊髓性肌萎缩症：来自三个亚太地区的1年数据

2021-10-20

soongzhihua (审核中...)

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#脊髓性肌萎缩#

NEJM：Risdiplam，脊髓性肌萎缩的第一个口服药

2022-02-05

soongzhihua (审核中...)

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#脊髓性肌萎缩#

JNNP:诺西那生钠治疗1型脊髓性肌萎缩症的的新生儿至青年数据——来自三个亚太地区的1年数据

2021-10-18

soongzhihua (审核中...)

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#脊髓性肌萎缩#

Evrysdi治疗脊髓性肌萎缩症（SMA），CHMP持积极意见

2021-12-08

soongzhihua (审核中...)

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#脊髓性肌萎缩#

JNNP:诺西那生钠治疗脊髓性肌萎缩症(SMA)的儿童的运动单位变化

2021-07-02

soongzhihua (审核中...)

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#脊髓性肌萎缩#

脊髓性肌萎缩Ⅲ型患者的剖宫产麻醉1例

2020-09-01

soongzhihua (审核中...)

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#脊髓性肌萎缩#

FDA批准口服性脊髓性肌萎缩症（SMA）药物Evrysdi

2021-03-27

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